Brasília – Gene therapy, a cutting-edge technique that modifies a patient’s genetic material to correct the cause of diseases, is advancing in Brazil. As O Globo reports, researchers are developing studies focused on conditions such as sickle cell disease and mucopolysaccharidosis (MPS), illustrating the growing national capacity to adopt frontier medical technologies.

Experts interviewed by the newspaper highlight that these therapies act directly on genetic mutations, offering the potential for long-term or even definitive cures. Brazilian research centers, including public institutions, are already engaged in pre-clinical and clinical projects aimed at adapting these treatments to local needs and expanding future access.

Despite these advances, challenges persist — particularly the high cost of development, the need for specialized infrastructure, and the ongoing construction of regulatory and ethical frameworks to ensure safety and equitable access for patients.

Source: O Globo

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